Using gene therapy to tackle complex brain disease

Substantial progress has been made in the development of treatments for a particular brain disease, thanks in part to an EU-funded project. The X-ALD project focused on achieving a better understanding of the pathogenic mechanisms leading to 'X-linked adrenoleukodystrophy', a disorder which results in the accumulation of long chain fatty acids in tissues throughout the body but especially in the central nervous system.

Further information: cordis.europa.eu